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Department of Health and Social Care
info: Department of Health and Social Care -
Health Research Authority
info: Health Research Authority -
Northern Ireland Rare Disease and Congenital Abnormality Registry (NIRADCAR)
info: Northern Ireland Rare Disease and Congenital Abnormality Registry (NIRADCAR) -

RD-IMAG (UK Rare Disease International Mirror and Action Group)
info: RD-IMAG (UK Rare Disease International Mirror and Action Group) -

Therapeutic Genomics CoRE
info: Therapeutic Genomics CoRE -

UK Platform of Nucleic Acid Therapy for rare disease treatment (UPNAT) Node
info: UK Platform of Nucleic Acid Therapy for rare disease treatment (UPNAT) Node