
Organisations
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Beacon for Rare Diseases
info: Beacon for Rare Diseases -

brainstrust
info: brainstrust -

Cambridge Rare DiseaseNetwork (CamRARE)
info: Cambridge Rare DiseaseNetwork (CamRARE) -
Cancer Research UK
info: Cancer Research UK -

Clever Cogs
info: Clever Cogs -

Costello Medical
info: Costello Medical -

Dravet Syndrome UK
info: Dravet Syndrome UK -

eXmoor Pharma
info: eXmoor Pharma -

Gene People
info: Gene People -

LAM Action
info: LAM Action -

LifeArc
info: LifeArc -

Metabolic Support
info: Metabolic Support -
National Institute for Health and Care Excellence (NICE)
info: National Institute for Health and Care Excellence (NICE) -

Nucleic Acid Therapy Accelerator
info: Nucleic Acid Therapy Accelerator -

Patient Led Research Hub
info: Patient Led Research Hub -

Prader Willi Syndrome Association UK
info: Prader Willi Syndrome Association UK -

PrimeRA Pharma Partners
info: PrimeRA Pharma Partners -

PTEN UK and Ireland Patient Group
info: PTEN UK and Ireland Patient Group -

Rare Disease Research Network
info: Rare Disease Research Network